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Latest News:
Sarepta Therapeutics announces plans to submit New Drug Application to FDA for Eteplirsen – A significant step for the Duchenne community 24 Jul 2013 | 08:56 pm
Today is a landmark day for the entire Duchenne community. Not too long ago, the Duchenne therapy landscape was a barren field with little to no life. Thanks to a commitment to our patients and the fi...
Connect Conference Recap 17 Jul 2013 | 01:54 am
This year's Connect Conference in Baltimore was incredibly informative and quite extensive. We packed our three days with the top experts in the Duchenne community. But, we know that some of you might...
Update from PPMD/FDA Meeting 17 Jul 2013 | 01:54 am
PPMD met with Dr. Janet Woodcock and leadership from the Office of New Drugs, Medical Policy and the Division of Neurology Products, as well as, staff from the Office of Strategic Programs, Office of ...
Update from Congressional Briefing 17 Jul 2013 | 01:53 am
A big day for Duchenne – Take action to help make it even more impactful! I had the pleasure to join other Duchenne advocates in Washington this week in an effort to bring attention to the need to ac...
PPMD Urges HHS Secretary to Update Organ Transplantation Policies to Ensure Pediatric Patients Have Access 17 Jul 2013 | 01:53 am
PPMD is urging the Secretary of Health and Human Services to update the nation's organ transplantation polices to ensure pediatric patients with rare diseases are not negatively impacted by outdated r...
End Duchenne eNews: Appreciating Parents 20 May 2013 | 06:20 pm
Catch up on the latest research and community updates in this month's End Duchenne eNews. Also meet our Featured Voice for May, 12-year-old Jack Knight.
2013 Connect Conference Agenda 20 May 2013 | 06:20 pm
PPMD’s Annual Connect Conference will be here before you know it! This summer we return to Baltimore, Maryland at the beautiful Marriott Waterfront with our most exciting and important agenda yet focu...
Drisapersen Update webinar with GSK 8 May 2013 | 08:46 pm
The purpose of the webinar is to update the Duchenne community about Phase II clinical trial results for GSK’s drisapersen drug for the treatment of Duchenne. GSK investigator John Kraus will present ...
DuchenneConnect Year-End Report 8 May 2013 | 08:46 pm
We had a busy and exciting year as we continue to expand our services to patients and families, as well as to researchers and clinicians. A big “thank you” to everyone who registered on DuchenneConnec...
New Mobile App - Locate Duchenne Clinical Trials 8 May 2013 | 08:46 pm
PPMD is thrilled to launch Duchenne Central! This new app for your smartphone allows you to search for Duchenne clinical trials and clinics near you or near a specific location. You can also keep trac...
